Table 2: Elevations in Liver Biochemical Tests Based on Thresholds
Table 2
Elevations in Liver Biochemical Tests Based on Thresholds
----------------------------------------------------------------------------------------------------------------------------------------------------
Risk Risk Risk
Difference Difference Difference
PL T1 T2 T1−PL T2−PL T2−T1
n/N (%) n/N (%) n/N (%) (95% CI) (95% CI) (95% CI)
(N=355) (N=318) (N=326) (N=673) (N=681) (N=644)
----------------------------------------------------------------------------------------------------------------------------------------------------
ALT
> 3x ULN 9/355 (2.5%) 8/318 (2.5%) 11/326 (3.4%) −0.0 (−2.4 − 2.4) 0.8 (−1.7 − 3.4) 0.9 (−1.8 − 3.5)
> 5x ULN 63/355 (17.7%) 53/318 (16.7%) 50/326 (15.3%) −1.1 (−6.8 − 4.6) −2.4 (−8.0 − 3.2) −1.3 (−7.0 − 4.3)
> 10x ULN 197/355 (55.5%) 183/318 (57.5%) 190/326 (58.3%) 2.1 (−5.4 − 9.6) 2.8 (−4.7 − 10.2) 0.7 (−6.9 − 8.4)
> 20x ULN 70/355 (19.7%) 60/318 (18.9%) 64/326 (19.6%) −0.9 (−6.8 − 5.1) −0.1 (−6.1 − 5.9) 0.8 (−5.3 − 6.9)
AST
> 3x ULN 12/355 (3.4%) 11/318 (3.5%) 16/326 (4.9%) 0.1 (−2.7 − 2.8) 1.5 (−1.5 − 4.5) 1.4 (−1.6 − 4.5)
> 5x ULN 93/355 (26.2%) 78/318 (24.5%) 89/326 (27.3%) −1.7 (−8.2 − 4.9) 1.1 (−5.6 − 7.8) 2.8 (−4.0 − 9.5)
> 10x ULN 236/355 (66.5%) 210/318 (66%) 208/326 (63.8%) −0.4 (−7.6 − 6.7) −2.7 (−9.8 − 4.5) −2.2 (−9.6 − 5.1)
> 20x ULN 10/355 (2.8%) 15/318 (4.7%) 9/326 (2.8%) 1.9 (−1.0 − 4.8) −0.1 (−2.5 − 2.4) −2.0 (−4.9 − 1.0)
Total Bilirubin
> 2x ULN 117/355 (33%) 81/318 (25.5%) 92/326 (28.2%) −7.5 (−14.3 − −0.6) −4.7 (−11.6 − 2.2) 2.7 (−4.1 − 9.6)
> 5x ULN 150/355 (42.3%) 154/318 (48.4%) 141/326 (43.3%) 6.2 (−1.3 − 13.7) 1.0 (−6.4 − 8.4) −5.2 (−12.9 − 2.5)
> 8x ULN 63/355 (17.7%) 63/318 (19.8%) 71/326 (21.8%) 2.1 (−3.9 − 8.0) 4.0 (−2.0 − 10.0) 2.0 (−4.3 − 8.2)
ALP
> 2x ULN 123/355 (34.6%) 120/318 (37.7%) 125/326 (38.3%) 3.1 (−4.2 − 10.4) 3.7 (−3.5 − 10.9) 0.6 (−6.9 − 8.1)
> 3x ULN 63/355 (17.7%) 57/318 (17.9%) 47/326 (14.4%) 0.2 (−5.6 − 6.0) −3.3 (−8.8 − 2.2) −3.5 (−9.2 − 2.2)
ALT or AST and Total Bilirubin
ALT > 3x ULN and Total 314/355 (88.5%) 285/318 (89.6%) 293/326 (89.9%) 1.2 (−3.5 − 5.9) 1.4 (−3.2 − 6.1) 0.3 (−4.4 − 4.9)
Bilirubin > 2x ULN
AST > 3x ULN and Total 326/355 (91.8%) 294/318 (92.5%) 301/326 (92.3%) 0.6 (−3.4 − 4.7) 0.5 (−3.6 − 4.6) −0.1 (−4.2 − 4.0)
Bilirubin > 2x ULN
ALT or AST > 3x ULN and 330/355 (93%) 298/318 (93.7%) 304/326 (93.3%) 0.8 (−3.0 − 4.5) 0.3 (−3.5 − 4.1) −0.5 (−4.3 − 3.4)
Total Bilirubin > 2x ULN
----------------------------------------------------------------------------------------------------------------------------------------------------
PL=Placebo, T1=Treatment 1, T2=Treatment 2, ALT=alanine aminotransferase, AST=aspartate aminotransferase, ALP=alkaline phosphatase;
N = number of applicable subjects in treatment arm; n = actual applicable observed number with values.